Empower & Inspire:

Understanding and Accelerating Research for Leigh Syndrome

 

 

Join Us Virtually On:

Tuesday, September 20, 2022

 

Brought to you by:

Cure Mito Foundation

&

integrative Cardiovascular Metabolism and Pathophysiology Laboratory (iCaMP) at Boston University

Registration is open. Please click HERE to register.

 

Confirmed Speakers

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Vamsi Mootha, MD

Keynote Speaker

Professor, Harvard Medical School

Professor, Massachusetts General Hospital

Investigator, Howard Hughes Medical Institute

Member, Broad Institute of MIT and Harvard

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Steven Gray, PhD

Introduction to Gene Therapy

Associate Professor, University of Texas Southwestern Medical Center 

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AlessandroPrigione, MD, PhD

Professor, University of Düsseldorf, Germany

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Michal Minczuk, PhD

Group Leader, University of Cambridge

Co-founder, Pretzel Therapeutics

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Simon Johnson, PhD

Assistant Professor, University of

Washington

PI, Seattle
Children’s Research Institute

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Saima Kayani, MD

Child Neurologist, UT Southwestern Medical Center

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Jessica L. Fetterman, PhD

Assistant Professor, Boston University School of Medicine

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Joe Bellucci, PhD 

Director, Scientific Partnerships, Rarebase

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Volkmar Weissig,ScD, PhD

Professor, Midwestern University

President, World Mitochondria Society

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Anne Murphy, PhD

Vice President of Biology, Cytokinetics

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Peter W. Stacpoole, PhD, MD

Professor, University of Florida

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Rhonda Facile, MS

Vice President, Partnerships and Development, CDISC

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Alexandre Bétourné, PhD, PharmD, PMP

Scientific Director, Critical Path Institute (C-Path)

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Angela Jocson, PSM

Senior Program Manager, AllStripes

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Rachel Kramer, PhD

Clinical Psychologist, Private Practice

Sponsors

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Agenda Includes:

 

Understanding Leigh Syndrome

 

Updates on Current Research 

 

Understanding the Drug Development Process: Roadmap, Clinical Trials, The Role of Patients in Accelerating Drug Development

 

Accelerating Research Through Data: Patient registries, Data sharing, Data standards

Introduction to Gene Therapy, Base Editing, Stem Cells, Organoids, Drug Repurposing

 

Caregiver Wellness

 

Discussion Sessions and Networking

 

More details coming soon!

For Speaking or Sponsoring Inquires, Please Reach Out To Us:

 info@curemito.org

If you're presenting, sponsoring, or attending, please click relevant graphic below to download and share!